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dc.contributor.authorRyan, M.
dc.contributor.authorDe Vivo, D.
dc.contributor.authorBertini, E.
dc.contributor.authorHwu, W.
dc.contributor.authorCrawford, T.
dc.contributor.authorSwoboda, K.
dc.contributor.authorFinkel, R.
dc.contributor.authorKirschner, J.
dc.contributor.authorKuntz, N.
dc.contributor.authorParsons, J.
dc.contributor.authorButterfield, R.
dc.contributor.authorTopaloglu, H.
dc.contributor.authorBen Omran, T.
dc.contributor.authorSansone, V.
dc.contributor.authorJong, Y.
dc.contributor.authorShu, F.
dc.contributor.authorFoster, R.
dc.contributor.authorBhan, I.
dc.contributor.authorFradette, S.
dc.contributor.authorFarwell, W.
dc.date.accessioned2021-06-02T10:39:55Z
dc.date.available2021-06-02T10:39:55Z
dc.date.issued2019
dc.identifier.issn0960-8966
dc.identifier.urihttp://dx.doi.org/10.1016/j.nmd.2019.06.518
dc.identifier.urihttp://hdl.handle.net/11655/23837
dc.language.isoen
dc.relation.isversionof10.1016/j.nmd.2019.06.518
dc.rightsAttribution 4.0 United States
dc.rightsinfo:eu-repo/semantics/openAccess
dc.rights.urihttps://creativecommons.org/licenses/by/4.0/
dc.titleNusinersen In Infants Who Initiate Treatment In A Presymptomatic Stage Of Spinal Muscular Atrophy: Interim Results From The Phase 2 Nurture Study
dc.typeinfo:eu-repo/semantics/article
dc.typeinfo:eu-repo/semantics/publishedVersion
dc.relation.journalNeuromuscular Disorders
dc.contributor.departmentÇocuk Sağlığı ve Hastalıkları
dc.identifier.volume29
dc.identifier.issue1
dc.description.indexWoS


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Attribution 4.0 United States
Except where otherwise noted, this item's license is described as Attribution 4.0 United States