Nusinersen In Infants Who Initiate Treatment In A Presymptomatic Stage Of Spinal Muscular Atrophy: Interim Results From The Phase 2 Nurture Study
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Date
2019Author
Ryan, M.
De Vivo, D.
Bertini, E.
Hwu, W.
Crawford, T.
Swoboda, K.
Finkel, R.
Kirschner, J.
Kuntz, N.
Parsons, J.
Butterfield, R.
Topaloglu, H.
Ben Omran, T.
Sansone, V.
Jong, Y.
Shu, F.
Foster, R.
Bhan, I.
Fradette, S.
Farwell, W.