Nusinersen In Infants Who Initiate Treatment In A Presymptomatic Stage Of Spinal Muscular Atrophy (Sma): Interim Results From The Phase 2 Nurture Study
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Göster/ Aç
Tarih
2019Yazar
Ryan, M. M.
De Vivo, D. C.
Bertini, E.
Hwu, W. L.
Crawford, T. O.
Swoboda, K. J.
Finkel, R. S.
Kirschner, J.
Kuntz, N. L.
Parsons, J.
Butterfield, R. J.
Topaloglu, H.
Ben Omran, T.
Sansone, V. A.
Jong, Y. J.
Shu, F.
Foster, R.
Bhan, I.
Fradette, S.
Farwell, W.