Browsing Dahili Tıp Bilimleri Bölümü by Author "Farwell, W."
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Nusinersen In Infants Who Initiate Treatment In A Presymptomatic Stage Of Spinal Muscular Atrophy (Sma): Interim Results From The Phase 2 Nurture Study
Ryan, M. M.; De Vivo, D. C.; Bertini, E.; Hwu, W. L.; Crawford, T. O.; Swoboda, K. J.; Finkel, R. S.; Kirschner, J.; Kuntz, N. L.; Parsons, J.; Butterfield, R. J.; Topaloglu, H.; Ben Omran, T.; Sansone, V. A.; Jong, Y. J.; Shu, F.; Foster, R.; Bhan, I.; Fradette, S.; Farwell, W. (2019) -
Nusinersen In Infants Who Initiate Treatment In A Presymptomatic Stage Of Spinal Muscular Atrophy: Interim Results From The Phase 2 Nurture Study
Ryan, M.; De Vivo, D.; Bertini, E.; Hwu, W.; Crawford, T.; Swoboda, K.; Finkel, R.; Kirschner, J.; Kuntz, N.; Parsons, J.; Butterfield, R.; Topaloglu, H.; Ben Omran, T.; Sansone, V.; Jong, Y.; Shu, F.; Foster, R.; Bhan, I.; Fradette, S.; Farwell, W. (2019)